National Gaucher Foundation 2021 Impact Report
The year 2021 took many of us on a roller... Read more
Gain Therapeutics, Inc. Announces Breakthrough Pre-Clinical Data of Novel Small Molecules for the Treatment of Parkinson’s Disease and Gaucher Disease
Study results demonstrate first small molecule approach to significantly reduce... Read more
7 Tips for Selecting Health Insurance When You Have a Pre-Existing Condition
UPDATED October 23, 2023 Health insurance serves as financial protection... Read more
Committing to Care, Access, Equity, and Research: NORD Announces 31 Rare Disease Centers of Excellence
NORD provides new designation to medical centers to define standards... Read more
How Systemic Inflammation Affects Your Brain & Central Nervous System
Bodies are like well-oiled machines, with many systems that work... Read more
Newborn Screening: What You Need to Know
People living with an inheritable disorder like Gaucher disease understand... Read more
Gain Therapeutics, Inc. Announces Positive Topline Data in Patient-derived iPSC Study Evaluating STAR Compounds as a Treatment for Gaucher and Parkinson’s Disease
GT-02287and GT-02329 compounds display positive effects on GCase activity and... Read more
9 Myths About Genetic Disease Carrier Screening
Health and family planning are deeply personal. Above all, everyone... Read more
AVROBIO Reports Second Quarter 2021 Financial Results and Provides Business Update
U.S. Food and Drug Administration granted Fast Track Designation to... Read more
Gaucher Disease and Reproductive Health
Living with a chronic hereditary condition like Gaucher disease can... Read more
