U.S. Food and Drug Administration (FDA) has accepted Prevail’s Investigational New Drug (IND) application for its lead gene therapy program, PR001. PR001 is a potentially disease-modifying, single-dose, AAV9-based gene therapy being developed for the treatment of Parkinson’s disease patients with a GBA1 mutation (PD-GBA).
Read the full press release:
https://www.businesswire.com/news/home/20190604006119/en/Prevail-Therapeutics-Announces-IND-Active-Phase-12